The Neuromuscular Disease Foundation in Great Neck Plaza, NY is dedicated to enhancing the quality of life for individuals living with GNE myopathy through critical research funding and advocacy efforts. Their International Gene Therapy Development Program (IGTDP) focuses on advancing treatments and a cure for the disease, while their virtual learning library offers a wealth of resources including speaker series events, podcasts, and webinars.
With a global impact spanning 50 countries and serving over 4,800 individuals annually, the foundation has funded $9 million towards GNE myopathy science and programs. Through the stories of patients like Tara, Amy, and Rushab, the foundation showcases the resilience and strength of those affected by the disease, highlighting the importance of ongoing research and support initiatives.
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