The AADC Research Trust is an International Patient Advocacy Organisation dedicated to representing children suffering from the ultra rare brain disorder Aromatic Amino Acid Decarboxylase deficiency (AADCd). They are at the forefront of pioneering Gene Therapy treatments and are actively involved in driving critical disease research, advancing treatment strategies, and improving diagnostic testing. With their remarkable work, they bring hope to many children living with rare diseases.
Through their conferences, webinars, and AADCd Family Workshop videos, The AADC Research Trust provides valuable information and support to families of children with AADCd. They help families recognize signs and symptoms, navigate the diagnostic odyssey, and access available support. The Trust also offers various ways for individuals to get involved and support their mission of raising global awareness and changing the lives of AADCd warriors.
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